mTOR inhibitors are used to treat certain types of cancer, organ transplant rejection, a genetic disorder called tuberous sclerosis complex (TSC), and more. These medications work by blocking a protein called mTOR (mammalian target of rapamycin), which helps regulate cell growth and survival. By inhibiting this protein, mTOR inhibitors can slow the growth of cancer cells, prevent the body from rejecting a transplanted organ, and reduce the growth of non-cancerous tumors in TSC. These medications come in different forms, including oral pills, liquids, and topical products. One example is sirolimus (Rapamune).
