Thalassemia Medications

Aqvesme is part of the Pyruvate Kinase Activator class and treats Thalassemia. Pyruvate kinase activators are used to treat hemolytic anemia. Pyruvate kinase activators work by increasing pyruvate kinase activity, and in turn, increasing the amount of energy available to cells. Aqvesme is only available as a brand name drug.

EXAGAMGLOGENE AUTOTEMCEL treats sickle cell disease. It may also be used to treat beta thalassemia. It works by helping your body make healthy red blood cells. These cells do not sickle. This can reduce symptoms of sickle cell disease, such as pain crises. Healthy red blood cells also reduce the need for blood transfusions in people with beta thalassemia.

BETIBEGLOGENE AUTOTEMCEL treats beta thalassemia. It works by helping your body make healthy red blood cells, which reduces the need for blood transfusions.