Medications for paroxysmal nocturnal hemoglobinuria (PNH) are used to treat this rare blood disorder. They help reduce the risk of hemolytic anemia and the need for blood transfusions. These medications work by blocking the complement system, which is part of your immune system that can attack your own red blood cells. Common classes include complement inhibitors. Complement inhibitors like Soliris (eculizumab), Ultomiris (ravulizumab), and Empaveli (pegcetacoplan) are usually given as injections. These treatments help manage PNH and its symptoms effectively.
