Glucosylceramide synthase (GCS) inhibitors are used to treat health conditions such as Gaucher disease type 1 and Pompe disease. One way GCS inhibitors work is by blocking the enzyme glucosylceramide synthase, which helps reduce the buildup of harmful substances in your cells. These medications are available in oral forms. Some examples include Zavesca, Yargesa, and Opfolda, which all contain the active ingredient miglustat.
