Lysosomal Storage Disease Medications

Popular Lysosomal Storage Disease Drugs

Popularity Drug Name Drug Class Price Price Trend
Enzyme Replacement Therapies 24,284
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ELIGLUSTAT is used for the long-term treatment of adults with Gaucher disease type I. Eliglustat is not used in certain people with Gaucher disease type 1. Your doctor will perform a test to make sure this medicine is right for you.
Enzyme Replacement Therapies 11,459
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AGALSIDASE BETA is used to replace an enzyme that is missing in patients with Fabry disease. It is not a cure.
Enzyme Replacement Therapies 1,859
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GALSULFASE is an enzyme replacement. It is used to treat the symptoms of mucopolysaccharidosis VI (also known as MPS VI or Maroteaux-Lamy syndrome). This medicine is not a cure.
Enzyme Replacement Therapies 863
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LARONIDASE is a drug that is used to replace an enzyme that is missing in patients with some forms of mucopolysaccharidosis I (MPS I). It is used to treat some of the symptoms of the disease. This medicine is not a cure.
Enzyme Replacement Therapies 3,207
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IDURSULFASE is used to replace an enzyme that is missing in patients with Hunter syndrome. It is not a cure.
Enzyme Replacement Therapies 1,021
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Enzyme Replacement Therapies 1,189
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ELOSULFASE ALFA is an enzyme replacement. It is used to treat the symptoms of Mucopolysaccharidosis type IVA (MPS IVA; Morquio A syndrome). This medicine is not a cure.
Enzyme Replacement Therapies 10,450
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Enzyme Replacement Therapies 789
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Taliglucerase alfa is a man-made form of an enzyme that is missing in patients with Gaucher's disease. It is used to treat the symptoms of Gaucher's disease. It is not a cure.
Enzyme Replacement Therapies 770
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ALGLUCOSIDASE ALFA is a drug that is used to replace an enzyme that is missing in patients with Pompe disease. It is not a cure.
Enzyme Replacement Therapies 1,400
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Velaglucerase alfa is a man-made form of an enzyme that is missing in patients with Gaucher's disease. It is used to treat the symptoms of Gaucher's disease. It is not a cure.
Enzyme Replacement Therapies 875
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IMIGLUCERASE is a man-made form of an enzyme that is missing in patients with Gaucher's disease. It is used to treat the symptoms of Gaucher's disease. It is not a cure.
GCS Inhibitors 28,010
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MIGLUSTAT helps to keep normal blood levels of an enzyme needed to breakdown fat in the body. It is used to treat type 1 Gaucher disease.
Cystine Depleting Agents 6,110
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Cystine Depleting Agents 120
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CYSTEAMINE breaks down cystine in the body. It is used to treat nephropathic cystinosis in children and adults. This medicine is not a cure.
Cystine Depleting Agents 5,090
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CYSTEAMINE breaks down cystine in the body. It is used to treat nephropathic cystinosis in children and adults. This medicine is not a cure.

Note: Popularity is based on total prescriptions for the brand and generic versions of each drug, regardless of the condition being treated. Some drugs are prescribed for multiple conditions.

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