What is Inherited Metabolic Diseases?

Inherited metabolic diseases are genetic conditions that affect the ability of enzymes in your body to convert various substances into others. In most metabolic disorders, health problems are due to a build up of toxic substances, or a reduced ability to make compounds your body needs to function.

Changes to your diet can help, as can replacement of enzymes in some cases. Gene therapy and bone marrow or organ transplant may also be recommended.

Popular Inherited Metabolic Diseases Drugs

Popularity Drug Name Drug Class Price
Enzyme Replacement Therapies 24,012 See Prices
Enzyme Replacement Therapies 22,483 See Prices
Enzyme Replacement Therapies 519 See Prices
see all 15 drugs

Note: Popularity is based on total prescriptions for the brand and generic versions of each drug, regardless of the condition being treated. Some drugs are prescribed for multiple conditions.

Inherited Metabolic Diseases Drug Classes

Copyright ©2016 GoodRx, Inc.

GoodRx is not sponsored by or affiliated with any of the pharmacies identified in its price comparisons. All trademarks, brands, logos and copyright images are property of their respective owners and rights holders and are used solely to represent the products of these rights holders. This information is for informational purposes only and is not meant to be a substitute for professional medical advice, diagnosis or treatment. GoodRx is not offering advice, recommending or endorsing any specific prescription drug, pharmacy or other information on the site. GoodRx provides no warranty for any of the pricing data or other information. Please seek medical advice before starting, changing or terminating any medical treatment.